A 19-year-old with cystic fibrosis (CF) is aiming to run the London Marathon to raise money for charity and awareness for the ...

In two randomised phase 3 studies involving 480 participants aged 12 years and over, ivacaftor/tezacaftor/vanzacaftor was ...

Vertex Pharmaceuticals (NasdaqGS:VRTX) announced that its cystic fibrosis treatment, ALYFTREK®, had received regulatory approval from the UK's MHRA, a significant milestone in expanding its market ...

UK MHRA approves Vertex’s Alyftrek, a once-daily next-in-class CFTR modulator to treat cystic fibrosis: London Monday, March 10, 2025, 10:00 Hrs [IST] Vertex Pharmaceuticals, a ...

H.C. Wainwright analyst Ed Arce lowered the firm’s price target on Arcturus Therapeutics (ARCT) to $60 from $63 and keeps a Buy rating on the ...

However, when Brandon Blackmon, 26, captured photos of his wife, Rinley Blackmon, 24, following their daughter's birth in June 2024, he opted for a very different style. Instead of taking the ...

A boy with a love of trains has gone behind the scenes at a railway signalling hub as a birthday treat.Zach from Walsall has cystic fibrosis and autism and his family said he developed a fascination ...

Sionna Therapeutics recently secured an initial public offering (IPO) of $191m on the Nasdaq stock exchange, signalling ...

The UK’s Medicines and Healthcare products Regulatory Agency (MHRA) has today approved Alyftrek (triple combination medicine ...

Plans to cut NIH funding undermine America's incredible record of medical success. Scientific research has helped win many ...

Infants with cystic fibrosis lack crucial “beneficial bacteria” in their gut, according to new research. Scientists say this ...

Approximately 1,000 new cases of Cystic Fibrosis are diagnosed each year that bring costly treatments to many families. The ...